orphan drug

RNA Concept 3D Render
Biotech

RNA biotech emerges with $52M and clinical rare disease asset

Arnatar currently touts seven assets, with six preclinical programs that range across cardiometabolic, inflammatory and CNS conditions.
Gabrielle Masson Aug 25, 2025 10:13am
Congress senate house government US
Favicon Fierce Pharma

Senate revives Orphan Cures Act in Trump's tax bill

Jun 30, 2025 10:09am
Combine

More collaborative FDA can accelerate rare disease R&D: report

Sep 13, 2024 5:00am
pipeline pipes RD research

As pharma eyes shiny obesity drugs, Vertex tops orphan drug list

Apr 24, 2024 12:01am
Pfizer

Pfizer punts pair of orphan drugs amid rare disease R&D rethink

Jan 31, 2023 9:15am
boardroom

Stealth granted FDA meeting to revive elamipretide filing

Jun 14, 2022 10:10am